On Wednesday we were saddened learned that double Nobel laureate Fred Sanger had died, so it was fitting that yesterday also saw the announcement of an important scientific advance that owes everything to the molecular biology revolution he helped to launch – one that may improve the lives of many thousands of people with Hemophilia A. … Continue reading Successful gene therapy for hemophilia A in dogs – humans next!
Several reports in the news over the past week have highlighted yet again the importance of animal research to medical advances. The BBC reports that gene therapy has been used successfully to treat a patient with severe β-thalassemia. β-thalassemia is an inherited disorder caused by mutations in the β-globin chain of haemoglobin that lead to … Continue reading Animal research: At the forefront of modern medicine
Leukemia is a cancer of the blood or bone marrow that affects over 200,000 Americans and still kills thousands every year despite the great progress made over recent decades in developing effective treatments for many leukemia types. When undergoing treatment for leukemia many patients require hematopoietic stem cell (HSC) transplantation to replace the blood stem … Continue reading Mice pave the way to a cord blood transplant advance